NEWS AND EVENTS

2019 Family Event

April 30, 2019
Join Us At the Zoo – REGISTRATION IS NOW CLOSED! – Due to overwhelming response, this event is at capacity. If you wish to be added to the waiting list, please fill out the form below, but please understand that… (read more)
NEWS AND EVENTS

BioMarin’s “PegPal” Receives FDA Approval

May 26, 2018

BioMarin announced this week that the FDA has approved its Palynziq™ injection for treatment of adults with Phenylketonuria (PKU). Formerly known during the clinical trials as PegPal, this is the first enzyme therapy to treat PKU and has been demonstrated … (read more)